Leber

Last fall, a team led by researchers at Children's Hospital of Philadelphia and University of Pennsylvania School of Medicine reported they had successfully injected a gene via a genetically engineered vector into the retinas of 12 patients suffering from a blindness-causing genetic disease called Leber's congenital amaurosis.

Study Shows Hope for Gene Therapy 2010

Although the patients had a rare form of blindness called Leber's congenital amaurosis, researchers believe the approach can ultimately be used for a broad spectrum of disorders, including retinitis pigmentosa and macular degeneration.

Berkshire Helps Concoct 2008

There has been a lot of ink recently about a new study where researchers used gene therapy to restore sight to patients suffering from a rare form of congenital blindness known as Leber congenital amaurosis.

Material World: Gene Therapy Restores Sight Eric Bland 2008

There has been a lot of ink recently about a new study where researchers used gene therapy to restore sight to patients suffering from a rare form of congenital blindness known as Leber congenital amaurosis.

Material World: April 2008 Tracy Staedter 2008

He then learned he suffered from a rare eye condition called Leber's Optic Neuropathy, which destroyed the central sight in both eyes.

CBC | Top Stories News 2011

Eighteen-month old Gavin Stevens, who is blind, was born with a rare retinal disease called Leber's Congenital Amaurosis.

The Orange County Register - News Headlines : Top Stories By LOU PONSI 2010

One of the first payoffs with gene therapy involves a relatively rare cause of blindness known as Leber congenital amaurosis.

The Augusta Chronicle admin 2010

Both Yokasta Urena and her daughter, Aolani, 4, live with the rare genetic disorder called Leber's congenital amaurosis that leaves them legally blind.

RNews - TOP STORIES 2009

Both Yokasta Urena and her daughter, Aolani, 4, live with the rare genetic disorder called Leber's congenital amaurosis that leaves them legally blind.

RNews - TOP STORIES 2009

Both Yokasta Urena and her daughter, Aolani, 4, live with the rare genetic disorder called Leber's congenital amaurosis that leaves them legally blind.

RNews - TOP STORIES 2009